Phil and Claire Drinkwater have raised more than £11,000 for charity since the loss of their 'joyful' son Jude ...

Rare diseases have become an attractive target for pharmaceutical companies both on the ASX and internationally.

Romi Loffler fears she will be among the hardest hit by East Renfrewshire Council's decision to means-test and charge for ...

Good morning, everyone, and welcome to the Anavex Life Sciences Fiscal 2025 First Quarter Conference Call. My name is Clint ...

People are more likely to have autism if they have related genetic disorders, such as fragile X syndrome, Rett syndrome, and tuberous sclerosis. Autism is also more likely due to a number of ...

According to the state Division of Developmental Disabilities, or DDD, nearly 4,000 people living with developmental ... as ...

Fintel reports that on February 11, 2025, Deutsche Bank initiated coverage of ACADIA Pharmaceuticals (NasdaqGS:ACAD) with a ...

If successful OPT-302 would be the first superior treatment in more than 15 years for wet-AMD, which affects around 3.5 million people in the US and Europe ... FDA and Health Canada for the treatment ...

According to the International Rett Syndrome Foundation, a diagnosis occurs approximately in one in 10,000 births worldwide. Life expectancy is also unknown, and on average, most people with the ...

Neuren’s flagship asset is Daybue, a treatment for Rett syndrome which has been licensed ... rebuilding gross margin story which I think people are just bored with now’’.

Neuren Pharmaceuticals (ASX: NEU) has announced that the US Food and Drug Administration (FDA) has granted Fast Track ...