Furthermore, 57% of participants showed cognitive and gait improvement ... a gene therapy for the enzyme deficiency known as Hurler syndrome. Per deal terms announced in January, Nippon Shinyaku ...

Data from the first patients enrolled into Regenxbio's trial of its gene therapy for rare inherited disease mucopolysaccharidosis type I (MPS I) – also known as Hurler syndrome – has shown the ...

By providing rapid IDUA delivery to the brain, RGX-111 could potentially help prevent the progression of cognitive deficits ... also known as Hunter syndrome, and RGX-111 for Mucopolysaccharidosis I ...

Milwaukee should turn its focus to former Texas Rangers hurler David Robertson. He and Kenley Jansen arguably are the best remaining hurlers on the open market right now for the bullpen.

One former member of the Boston Red Sox likely is going to need to find a new home in the near future. The Los Angeles Dodgers officially announced their signing of two-time All-Star Kirby Yates ...

Emma Ward, who has Hurler syndrome, was unable to charge her wheelchair or attend college after Storm Eowyn hit. Emma told The Irish Sun: “It was unimaginable to be honest. It was a long 13 days.” ...

A former All Ireland-winning hurler has died in an incident in Co Galway while cleaning up storm debris near his home. Michael Coleman, who won an All-Ireland with Galway in 1988, died following ...

Living with the genetic condition that affects the brain, lungs and other organs, means Emma relies on a wheelchair. Forced to use a walking aid, the Galway native said she hadn’t felt so much ...

The Chicago Cubs have a lot of talent and should be able to compete for the top spot in the National League Central in 2025. The Milwaukee Brewers earned the top spot in each of the last two years ...

The Cardinals followed that up by signing veteran hurler Nick Anderson to a minor league deal, as shared by MLB Trade Rumors' Steve Adams. "The Cardinals announced Friday that they’ve signed ...

San Diego Padres star pitcher Yu Darvish recently had a chance to detail his thoughts on a major move that took place in free agency this offseason. Per Jeff Sanders of The San Diego Tribune ...

That partner, Japan’s Nippon Shinyaku, is handing over $110 million upfront to lead on the commercialization of two gene therapies—RGX-121 for Hunter syndrome and RGX-111 for Hurler syndrome.